7,000 #rarediseases impact 30M Americans, yet only 5% have FDA-approved treatments. Since the Orphan Drug Act, 5,000+ new ODD-approved drugs & biologics have emerged. As part of this journey, we're committed to bringing hope to the 95% waiting for a cu
This is a reflection of the substantial growth in orphan drug designations and approvals by the FDA and other regulatory bodies since the US Orphan Drug Act in 1983 (source: https://t.co/0Y4pt0DaIc) https://t.co/pBQ4oqWbOF
🤔 Do you know what #orphandrugs are? We are sharing a scientific paper where, through data provided by the FDA, we can see how it changes the development of therapies for #rarediseases. 💊 📌 https://t.co/17PuMldOCr #fundedbyCDTI https://t.co/FyblAYJDxp
🤔 ¿Sabes qué son los #medicamentoshuérfanos? Os compartimos un paper científico donde, a través de datos aportados por la FDA, podemos ver como cambia el desarrollo de terapias para #enfermedadesraras. 💊 📌 https://t.co/17PuMldOCr #financiadoporCDTI https: