1,949 followers
@alsadvocacy Re-sharing this article because I think it is really good: https://t.co/9f0swFHpH8
11,948 followers
Interesting insights into WHY a natural history study is so important. Our ALS snapshots in time are not enough.
1,949 followers
Excellent example of public (NIH)-private-patient advocacy group collaboration, including on NHS and strategic planning. I connected with this group in my FDA rep days. Taught me how to plan partnerships. https://t.co/9f0swFHpH8
3,974 followers
Fostering collaborative research for rare genetic disease: the example of niemann-pick type C disease https://t.co/X9SXBdOfyh …