Toward patient-centered treatment goals for duchenne muscular dystrophy: insights from the “Your Voice” study

It's critical to publish "patient voice" to help this input inform all - thx @JettFoundation for leading this important study in #Duchenne & inviting me to provide regulatory perspective + @EngageHealthInc for making these methods available to #raredis

Toward patient-centered treatment goals for duchenne muscular dystrophy: insights from the “Your Voice” study https://t.co/od4qzIpTz2