A systematic overview of rare disease patient registries: challenges in design, quality management, and maintenance
Article in Orphanet Journal of Rare Diseases (May 2023)
The most recent citing publications are shown below. View all 8 publications that cite this research output on Dimensions.
Article in Orphanet Journal of Rare Diseases (May 2023)
Article in BMJ Open (September 2022)
Article in Molecular Genetics and Metabolism (October 2021)