Zinc finger nucleases for targeted mutagenesis and repair of the sickle-cell disease mutation: An in-silico study

@thecuresci translation to a home grown #CRISPER based gene therapeutic cure for sickle cell anemia is the path for equitable access https://t.co/60wcBZeexx

@NIHDirector @nih_nhlbi I argue that the best way to make this gene therapy more available and affordable....is to have it done in one step--insitu. This can be achieved via bone marrow infusions of the vector. https://t.co/60wcBZeexx