Rare Diseases Clinical Trials Toolbox - Public resources and main considerations to set up a clinical trial on medicinal products for humans in Europe
Preprint in medRxiv (February 2024)
The most recent citing publications are shown below. View all 22 publications that cite this research output on Dimensions.
Preprint in medRxiv (February 2024)
Article in The Journal of Clinical Endocrinology & Metabolism (January 2024)
Article in Orphanet Journal of Rare Diseases (December 2023)