RT @UCSFmac: Impaired β-glucocerebrosidase activity & processing in FTD due to progranulin mutations. Grn−/− mice had lower β-glucocerebros…
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Impaired β-glucocerebrosidase activity & processing in FTD due to progranulin mutations. Grn−/− mice had lower β-glucocerebrosidase activity than wild-type littermates – corrected by AAV-progranulin gene therapy. https://t.co/HDyrb6gMLi @SalvoSpinaSF @
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RT @UCSFmac: Impaired β-glucocerebrosidase activity and processing in frontotemporal dementia due to progranulin mutations. PGRN insufficie…
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Impaired β-glucocerebrosidase activity and processing in frontotemporal dementia due to progranulin mutations. PGRN insufficiency impairs β-glucocerebrosidase activity in the brain. Effect is strongest in neurons. @RobersonLabUAB @SalvoSpinaSF @grinberg_t