Lifelong Outcomes of Systemic Adeno-Associated Virus Micro-Dystrophin Gene Therapy in a Murine Duchenne Muscular Dystrophy Model
Article in Human Gene Therapy (May 2023)
The most recent citing publications are shown below. View all 18 publications that cite this research output on Dimensions.
Changes in Myonuclear Number During Postnatal Growth – Implications for AAV Gene Therapy for Muscular Dystrophy
Article in Journal of Neuromuscular Diseases (November 2021)
CFTR corrector C17 is effective in muscular dystrophy, in vivo proof of concept in LGMDR3
Article in Human Molecular Genetics (September 2021)