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Impact of miglustat on evolution of atypical presentation of late-infantile-onset Niemann-Pick disease type C with… https://t.co/dfCo7h5kId
Impact of miglustat on evolution of atypical presentation of late-infantile-onset Niemann-Pick disease type C with… https://t.co/dfCo7h5kId
Niemann–Pick disease type C patient has improved #neurological manifestations & #epilepsy control after miglustat: https://t.co/VtpouQ5H6X
Miglustat improved the neurological status of our patient, including #seizure control: https://t.co/VtpouQ5H6X