Emerging drugs for the treatment of progressive familial intrahepatic cholestasis: a focus on phase II and III trials.
Article in Expert Opinion on Emerging Drugs (April 2024)
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Gray Platelet Syndrome: Diagnosis and Management
Book chapter (December 2023)
Two novel mutations in VPS33B gene cause a milder ARC syndrome with prolonged survival in a 12-year-old patient: Case report
Article in Frontiers in Pediatrics (December 2022)