Draft Guidance for Industry Duchenne Muscular Dystrophy, Becker Muscular Dystrophy, and Related Dystrophinopathies – Developing Potential Treatments for the Entire Spectrum of Disease
Article in Journal of Neuromuscular Diseases (March 2024)
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Article in Journal of Neuromuscular Diseases (March 2024)
Article in Neurology and Therapy (June 2023)
Article in Cureus (May 2023)