Title |
Improved upper limb function in non-ambulant children with SMA type 2 and 3 during nusinersen treatment: a prospective 3-years SMArtCARE registry study
|
---|---|
Published in |
Orphanet Journal of Rare Diseases, October 2022
|
DOI | 10.1186/s13023-022-02547-8 |
Pubmed ID | |
Authors |
Astrid Pechmann, Max Behrens, Katharina Dörnbrack, Adrian Tassoni, Franziska Wenzel, Sabine Stein, Sibylle Vogt, Daniela Zöller, Günther Bernert, Tim Hagenacker, Ulrike Schara-Schmidt, Maggie C. Walter, Astrid Bertsche, Katharina Vill, Matthias Baumann, Manuela Baumgartner, Isabell Cordts, Astrid Eisenkölbl, Marina Flotats-Bastardas, Johannes Friese, René Günther, Andreas Hahn, Veronka Horber, Ralf A. Husain, Sabine Illsinger, Jörg Jahnel, Jessika Johannsen, Cornelia Köhler, Heike Kölbel, Monika Müller, Arpad von Moers, Annette Schwerin-Nagel, Christof Reihle, Kurt Schlachter, Gudrun Schreiber, Oliver Schwartz, Martin Smitka, Elisabeth Steiner, Regina Trollmann, Markus Weiler, Claudia Weiß, Gert Wiegand, Ekkehard Wilichowski, Andreas Ziegler, Hanns Lochmüller, Janbernd Kirschner |
X Demographics
Geographical breakdown
Country | Count | As % |
---|---|---|
Unknown | 2 | 100% |
Demographic breakdown
Type | Count | As % |
---|---|---|
Members of the public | 2 | 100% |
Mendeley readers
Geographical breakdown
Country | Count | As % |
---|---|---|
Unknown | 29 | 100% |
Demographic breakdown
Readers by professional status | Count | As % |
---|---|---|
Student > Master | 5 | 17% |
Other | 1 | 3% |
Student > Bachelor | 1 | 3% |
Librarian | 1 | 3% |
Student > Ph. D. Student | 1 | 3% |
Other | 3 | 10% |
Unknown | 17 | 59% |
Readers by discipline | Count | As % |
---|---|---|
Medicine and Dentistry | 5 | 17% |
Pharmacology, Toxicology and Pharmaceutical Science | 4 | 14% |
Biochemistry, Genetics and Molecular Biology | 2 | 7% |
Neuroscience | 2 | 7% |
Linguistics | 1 | 3% |
Other | 2 | 7% |
Unknown | 13 | 45% |