Efficacy confirmation study of aceneuramic acid administration for GNE myopathy in Japan
Article in Orphanet Journal of Rare Diseases (August 2023)
The most recent citing publications are shown below. View all 5 publications that cite this research output on Dimensions.
Article in Orphanet Journal of Rare Diseases (August 2023)
Article in Journal of Neuromuscular Diseases (July 2023)
Preprint in Research Square (May 2023)