Long term peripheral AAV9-SMN gene therapy promotes survival in a mouse model of spinal muscular atrophy
Article in Human Molecular Genetics (December 2023)
The most recent citing publications are shown below. View all 54 publications that cite this research output on Dimensions.
Article in Human Molecular Genetics (December 2023)
Article in Human Molecular Genetics (November 2023)
Preprint in bioRxiv (June 2023)