Characteristics of drugs for ultra-rare diseases versus drugs for other rare diseases in HTA submissions made to the CADTH CDR

RT @fedegio3: There is rare and rare...how distinguishing ultra-rare diseases from more prevalent rare diseases would improve evaluation/ac…

There is rare and rare...how distinguishing ultra-rare diseases from more prevalent rare diseases would improve evaluation/access of/to orphan drugs #RareDisease #OrphanDrugs #access2meds https://t.co/15FbU1q3cb

RT @MD_Briggs: Should 'ultra-rare diseases' be considered a separate entity from a health economics/technology assessment perspective? An…

RT @MD_Briggs: Should 'ultra-rare diseases' be considered a separate entity from a health economics/technology assessment perspective? An…