RT @fedegio3: There is rare and rare...how distinguishing ultra-rare diseases from more prevalent rare diseases would improve evaluation/ac…
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There is rare and rare...how distinguishing ultra-rare diseases from more prevalent rare diseases would improve evaluation/access of/to orphan drugs #RareDisease #OrphanDrugs #access2meds https://t.co/15FbU1q3cb
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RT @MD_Briggs: Should 'ultra-rare diseases' be considered a separate entity from a health economics/technology assessment perspective? An…
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RT @MD_Briggs: Should 'ultra-rare diseases' be considered a separate entity from a health economics/technology assessment perspective? An…