Enzyme replacement therapy reduces the risk for wheelchair dependency in adult Pompe patients

Published in @ojrarediseases, enzyme replacement therapy (ERT) can positively affect both respiratory and motor outcomes of Pompe patients. Pompe disease is an autosomal recessive metabolic disorder which damages muscle and nerve cells in the body. https:/

RT @ojrarediseases: Enzyme replacement therapy reduces the risk for wheelchair dependency in adult #Pompe patients #RareDisease https://t…

RT @ojrarediseases: Enzyme replacement therapy reduces the risk for wheelchair dependency in adult #Pompe patients #RareDisease https://t…

Enzyme replacement therapy reduces the risk for wheelchair dependency in adult #Pompe patients #RareDisease https://t.co/fOK8F3BbMD