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Design of patient-focused registry for follow-up post- #genetherapy. Article co-authored by @Telethonitalia colleagues. #RareDisease https://t.co/XmCvPQmlMb #
Design of patient-focused registry for follow-up post- #genetherapy. Article co-authored by @Telethonitalia colleagues. #RareDisease https://t.co/XmCvPQmlMb #
Gene therapy in rare diseases: the benefits and challenges of developing a patient-centric registry for Strimvelis in ADA-SCID. https://t.co/1jpTRjPjFM