Orphanet-Italia, 05 Nov 2015 EFFICACIA DELLA TERAPIA ENZIMATICA SOSTITUTIVA CON AGALSIDASI ALFA: EFFETTI A LIVELLO CARDIACO DOPO 10 ANNI DI TRATTAMENTO
Neurogenetica Clinica Pisa, 27 Oct 2015 Great article just came out: Effectiveness of agalsidase alfa enzyme replacement in Fabry disease: cardiac outcomes after 10…