Long-Term Outcome of Infantile Onset Pompe Disease Patients Treated with Enzyme Replacement Therapy - Data from a German-Austrian Cohort
Article in Journal of Neuromuscular Diseases (January 2024)
The most recent citing publications are shown below. View all 20 publications that cite this research output on Dimensions.
Are Anti-rhGAA Antibodies a Determinant of Treatment Outcome in Adults with Late-Onset Pompe Disease? A Systematic Review
Article in Biomolecules (September 2023)
Unusual Evolution of Hypertrophic Cardiomyopathy in Non-Compaction Myocardium in a Pompe Disease Patient
Article in Journal of Clinical Medicine (March 2023)