Lentiviral Gene Therapy for Mucopolysaccharidosis II with Tagged Iduronate 2-Sulfatase Prevents Life-Threatening Pathology in Peripheral Tissues But Fails to Correct Cartilage
Article in Human Gene Therapy (February 2024)
The most recent citing publications are shown below. View all 26 publications that cite this research output on Dimensions.
Article in Human Gene Therapy (February 2024)
Article in International Journal of Otolaryngology-Head and Neck Surgery (November 2023)
Article in Journal of Personalized Medicine (March 2023)