The Clinical Findings, Pathogenic Variants, and Gene Therapy Qualifications Found in a Leber Congenital Amaurosis Phenotypic Spectrum Patient Cohort
Article in International Journal of Molecular Sciences (January 2024)
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Article in International Journal of Molecular Sciences (January 2024)
Article in Trends in Genetics (November 2023)
Article in International Journal of Molecular Sciences (September 2023)