Efficacy and safety of compassionate use for rare diseases: a scoping review from 1991 to 2022
Article in Orphanet Journal of Rare Diseases (November 2023)
The most recent citing publications are shown below. View all 8 publications that cite this research output on Dimensions.
Article in Orphanet Journal of Rare Diseases (November 2023)
Article in Heart Failure Reviews (September 2023)
Article in Journal of Central South University. Medical sciences. (April 2023)