A Rare Public Health Challenge
NIH Director's Blog,
Caption: More than 10,000 rare diseases affect nearly 400 million people across the globe. Credit: Christina Loccke, Lindsey…
Partnership to Expand Effective Gene Therapies for Rare Diseases
NIH Director's Blog,
Rare diseases aren’t so rare. Collectively, up to 30 million Americans, many of them children, are born with one of the…
NIH study suggests people with rare diseases face significantly higher health care costs
NIH News Releases,
Research provides new evidence of the potential impact of rare diseases on public health.