An ASO therapy for Angelman syndrome that targets an evolutionarily conserved region at the start of the UBE3A-AS transcript
Article in Science Translational Medicine (March 2023)
The most recent citing publications are shown below. View all 15 publications that cite this research output on Dimensions.
Article in Science Translational Medicine (March 2023)
Article in Molecular Genetics & Genomic Medicine (February 2022)
Preprint in bioRxiv (July 2021)