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Adult Niemann-Pick disease type C in France: clinical phenotypes and long-term miglustat treatment effect https://t.co/7ixJXcw3i7 #niemann-pick #lysosomal #raredesease #eerr
Adult Niemann-Pick disease type C in France: clinical phenotypes and long-term miglustat treatment effect https://t.co/7ixJXcw3i7 #niemann-pick #lysosomal #raredesease #eerr
Adult Niemann-Pick disease type C in France: clinical phenotypes and long-term miglustat treatment effect https://t.co/NJ6ILSBEfa
PubMed: Adult Niemann-Pick disease type C in France: clinical phenotypes and long-term miglustat treatment effect. https://t.co/hvGP6BdQ14